{"id":15344,"date":"2022-03-16T10:38:18","date_gmt":"2022-03-16T07:38:18","guid":{"rendered":"https:\/\/www.qatifscience.com\/?p=15344"},"modified":"2022-03-16T10:38:18","modified_gmt":"2022-03-16T07:38:18","slug":"%d8%a7%d9%84%d8%b9%d9%84%d8%a7%d8%ac%d8%a7%d8%aa-%d8%a7%d9%84%d8%ac%d9%8a%d9%86%d9%8a%d8%a9-%d9%84%d9%85%d8%b1%d8%b6-%d8%a7%d9%84%d8%ae%d9%84%d8%a7%d9%8a%d8%a7-%d8%a7%d9%84%d9%85%d9%86%d8%ac%d9%84","status":"publish","type":"post","link":"https:\/\/www.qatifscience.com\/?p=15344","title":{"rendered":"\u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u062c\u064a\u0646\u064a\u0629 \u0644\u0645\u0631\u0636 \u0627\u0644\u062e\u0644\u0627\u064a\u0627 \u0627\u0644\u0645\u0646\u062c\u0644\u064a\u0629 \u062a\u0623\u062a\u064a \u0645\u0639 \u0627\u0644\u0623\u0645\u0644 \u0648\u0627\u0644\u062a\u062d\u062f\u064a\u0627\u062a (\u0627\u0644\u062c\u0632\u0621 1 \u0645\u0646 2) &#8211; \u062a\u0631\u062c\u0645\u0629* \u0645\u062d\u0645\u062f \u062c\u0648\u0627\u062f 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\u0627\u0644\u0623\u0645\u0631\u0627\u0636\u060c \u0628\u0625\u062f\u062e\u0627\u0644 \u0627\u0644\u062d\u0645\u0636 \u0627\u0644\u0646\u0648\u0648\u064a \u0628\u0634\u0643\u0644 \u062f\u0627\u0626\u0645 \u0641\u064a \u0627\u0644\u0645\u062e\u0637\u0637 \u0627\u0644\u062c\u064a\u0646\u064a \u0644\u0644\u062e\u0644\u064a\u0629. \u062b\u0645 \u064a\u062a\u062f\u0627\u062e\u0644 \u0627\u0644\u062d\u0645\u0636 \u0627\u0644\u0646\u0648\u0648\u064a \u0627\u0644\u0631\u064a\u0628\u064a \u0627\u0644\u0635\u063a\u064a\u0631 \u0645\u0639 \u0625\u0646\u062a\u0627\u062c \u0628\u0631\u0648\u062a\u064a\u0646 \u064a\u0645\u0646\u0639 \u0635\u0646\u0639 \u0627\u0644\u0647\u064a\u0645\u0648\u063a\u0644\u0648\u0628\u064a\u0646 \u0627\u0644\u062c\u0646\u064a\u0646\u064a. \u0648\u0628\u0645\u062c\u0631\u062f \u062d\u0638\u0631 \u0647\u0630\u0627 \u0627\u0644\u0628\u0631\u0648\u062a\u064a\u0646\u060c \u064a\u062a\u0645 \u062a\u0634\u063a\u064a\u0644 \u0625\u0646\u062a\u0627\u062c \u0627\u0644\u0647\u064a\u0645\u0648\u063a\u0644\u0648\u0628\u064a\u0646 \u0627\u0644\u062c\u0646\u064a\u0646\u064a \u0645\u0631\u0629 \u0623\u062e\u0631\u0649. \u0648\u0645\u062b\u0644 \u062a\u0634\u063a\u064a\u0644 \u0635\u0646\u0628\u0648\u0631\u060c \u064a\u0645\u0643\u0646 \u0623\u0646 \u064a\u062a\u062f\u0641\u0642 \u062a\u064a\u0627\u0631 \u0645\u0633\u062a\u0645\u0631 \u0645\u0646 \u0627\u0644\u0647\u064a\u0645\u0648\u063a\u0644\u0648\u0628\u064a\u0646 \u0627\u0644\u0635\u062d\u064a \u0625\u0644\u0649 \u0645\u062c\u0631\u0649 \u0627\u0644\u062f\u0645\u060c \u0645\u0645\u0627 \u064a\u0639\u0648\u0636 \u0639\u0646 \u0627\u0644\u0634\u0643\u0644 \u0627\u0644\u0645\u0639\u0637\u0648\u0628.<\/p>\n<p>\u0648\u0642\u062f \u0623\u0638\u0647\u0631\u062a \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0623\u0648\u0644\u064a\u0629 \u0627\u0644\u0635\u0627\u062f\u0631\u0629 \u0641\u064a \u064a\u0646\u0627\u064a\u0631 2021 \u0623\u0646 \u0627\u0644\u0639\u0644\u0627\u062c \u0633\u0627\u0639\u062f \u0633\u062a\u0629 \u0645\u0631\u0636\u0649 \u0628\u0627\u0644\u062e\u0644\u0627\u064a\u0627 \u0627\u0644\u0645\u0646\u062c\u0644\u064a\u0629 \u0639\u0644\u0649 \u0635\u0646\u0639 \u0627\u0644\u0647\u064a\u0645\u0648\u063a\u0644\u0648\u0628\u064a\u0646 \u0627\u0644\u062c\u0646\u064a\u0646\u064a\u060c \u0648\u0641\u0642\u0627 \u0644\u0645\u0627 \u0630\u0643\u0631\u062a\u0647 \u0627\u0644\u062f\u0643\u062a\u0648\u0631\u0629 \u0625\u0633\u0631\u064a\u0643 \u0648\u0632\u0645\u0644\u0627\u0624\u0647\u0627 \u0641\u064a \u0645\u062c\u0644\u0629 \u0646\u064a\u0648 \u0625\u0646\u062c\u0644\u0627\u0646\u062f \u0627\u0644\u0637\u0628\u064a\u0629. \u0648\u0623\u062b\u0646\u0627\u0621 \u0641\u062a\u0631\u0629 \u0627\u0644\u0645\u062a\u0627\u0628\u0639\u0629\u060c \u0627\u0644\u062a\u064a \u062a\u0631\u0627\u0648\u062d\u062a \u0645\u0646 \u0639\u062f\u0629 \u0623\u0634\u0647\u0631 \u0625\u0644\u0649 \u0623\u0643\u062b\u0631 \u0645\u0646 \u0639\u0627\u0645\u064a\u0646\u060c \u062a\u0645 \u062a\u0642\u0644\u064a\u0644 \u0623\u0639\u0631\u0627\u0636 \u0627\u0644\u0645\u0631\u0636\u0649 \u0623\u0648 \u0627\u0644\u0642\u0636\u0627\u0621 \u0639\u0644\u064a\u0647\u0627. \u0648\u0642\u0627\u0645 \u0627\u0644\u0641\u0631\u064a\u0642 \u0628\u062a\u0648\u0633\u064a\u0639 \u0627\u0644\u062a\u062c\u0631\u0628\u0629 \u0644\u062a\u0634\u0645\u0644 \u0627\u0644\u0645\u0632\u064a\u062f \u0645\u0646 \u0627\u0644\u0645\u0631\u0636\u0649 \u0648\u0625\u062c\u0631\u0627\u0621 \u0645\u0632\u064a\u062f \u0645\u0646 \u0627\u0644\u0627\u062e\u062a\u0628\u0627\u0631\u0627\u062a \u0644\u0644\u0639\u0644\u0627\u062c.<\/p>\n<figure id=\"attachment_15346\" aria-describedby=\"caption-attachment-15346\" style=\"width: 300px\" class=\"wp-caption aligncenter\"><img loading=\"lazy\" decoding=\"async\" class=\"size-medium wp-image-15346\" src=\"https:\/\/www.qatifscience.com\/wp-content\/uploads\/2022\/03\/100-genetics_spotlight-esrick_inline2_headhshot-300x300.jpg\" alt=\"\" width=\"300\" height=\"300\" srcset=\"https:\/\/www.qatifscience.com\/wp-content\/uploads\/2022\/03\/100-genetics_spotlight-esrick_inline2_headhshot-300x300.jpg 300w, https:\/\/www.qatifscience.com\/wp-content\/uploads\/2022\/03\/100-genetics_spotlight-esrick_inline2_headhshot-150x150.jpg 150w, https:\/\/www.qatifscience.com\/wp-content\/uploads\/2022\/03\/100-genetics_spotlight-esrick_inline2_headhshot-75x75.jpg 75w, https:\/\/www.qatifscience.com\/wp-content\/uploads\/2022\/03\/100-genetics_spotlight-esrick_inline2_headhshot-165x165.jpg 165w, https:\/\/www.qatifscience.com\/wp-content\/uploads\/2022\/03\/100-genetics_spotlight-esrick_inline2_headhshot-205x205.jpg 205w, https:\/\/www.qatifscience.com\/wp-content\/uploads\/2022\/03\/100-genetics_spotlight-esrick_inline2_headhshot-330x330.jpg 330w, https:\/\/www.qatifscience.com\/wp-content\/uploads\/2022\/03\/100-genetics_spotlight-esrick_inline2_headhshot-525x525.jpg 525w, https:\/\/www.qatifscience.com\/wp-content\/uploads\/2022\/03\/100-genetics_spotlight-esrick_inline2_headhshot.jpg 680w\" sizes=\"auto, (max-width: 300px) 100vw, 300px\" \/><figcaption id=\"caption-attachment-15346\" class=\"wp-caption-text\"><span style=\"color: #0000ff; font-size: 8pt;\">\u0637\u0628\u064a\u0628\u0629 \u0627\u0644\u0623\u0637\u0641\u0627\u0644 \u0627\u0644\u062f\u0643\u062a\u0648\u0631\u0629 \u0625\u064a\u0631\u064a\u0643\u0627 \u0625\u0633\u0631\u064a\u0643 \u0645\u062a\u062d\u0645\u0633\u0629 \u0644\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u062c\u064a\u0646\u064a\u0629 \u0627\u0644\u0645\u062d\u062a\u0645\u0644\u0629 \u0648\u0644\u0643\u0646\u0647\u0627 \u062d\u0631\u064a\u0635\u0629 \u0639\u0644\u0649 \u0639\u062f\u0645 \u0627\u0644\u0645\u0628\u0627\u0644\u063a\u0629 \u0641\u064a \u0627\u0644\u0646\u062a\u0627\u0626\u062c \u0627\u0644\u0645\u0628\u0643\u0631\u0629. \u062a\u0645 \u0627\u0644\u062d\u0635\u0648\u0644 \u0639\u0644\u0649 \u0627\u0644\u0635\u0648\u0631\u0629 \u0628\u0625\u0630\u0646 \u0645\u0646 \u0645\u0633\u062a\u0634\u0641\u0649 \u0628\u0648\u0633\u0637\u0646 \u0644\u0644\u0623\u0637\u0641\u0627\u0644.<\/span><\/figcaption><\/figure>\n<p>\u0648\u064a\u062e\u062a\u0628\u0631 \u0627\u0644\u0639\u0644\u0645\u0627\u0621 \u0637\u0631\u0642\u0627 \u0623\u062e\u0631\u0649 \u0644\u0645\u0639\u0627\u0644\u062c\u0629 \u0627\u0644\u062e\u0644\u0627\u064a\u0627 \u0627\u0644\u0645\u0646\u062c\u0644\u064a\u0629 \u0639\u0646 \u0637\u0631\u064a\u0642 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a \u0623\u064a\u0636\u0627. \u0648\u062a\u0642\u0648\u0645 \u0634\u0631\u0643\u0629 \u0644\u0644\u062a\u0643\u0646\u0648\u0644\u0648\u062c\u064a\u0627 \u0627\u0644\u062d\u064a\u0648\u064a\u0629 \u062a\u0633\u0645\u0649 &#8220;\u0628\u0644\u0648\u0628\u064a\u0631\u062f \u0628\u0627\u064a\u0648&#8221; (bluebird bio) \u0628\u0627\u062e\u062a\u0628\u0627\u0631 \u0646\u0647\u062c \u064a\u0642\u062f\u0645 \u0646\u0633\u062e\u0629 \u0648\u0638\u064a\u0641\u064a\u0629 \u0645\u0646 \u062c\u064a\u0646 \u0648\u062d\u062f\u0629 \u0627\u0644\u0647\u064a\u0645\u0648\u063a\u0644\u0648\u0628\u064a\u0646 \u0627\u0644\u0641\u0631\u0639\u064a\u0629 \u0628\u064a\u062a\u0627 \u0644\u0644\u0645\u0631\u0636\u0649. \u0648\u064a\u0633\u062a\u0639\u062f \u0641\u0631\u064a\u0642 \u0622\u062e\u0631 \u0644\u0628\u062f\u0621 \u062a\u062c\u0631\u0628\u0629 \u0645\u0646 \u0634\u0623\u0646\u0647\u0627 \u062a\u062d\u0631\u064a\u0631 \u0647\u0630\u0627 \u0627\u0644\u062c\u064a\u0646 \u0645\u0628\u0627\u0634\u0631\u0629 \u0628\u0627\u0633\u062a\u062e\u062f\u0627\u0645 \u0643\u0631\u064a\u0633\u0628\u0631\/\u0643\u0627\u06339 [\u0662].<\/p>\n<p><span style=\"color: #0000ff;\">*\u062a\u0645\u062a \u0627\u0644\u062a\u0631\u062c\u0645\u0629 \u0628\u062a\u0635\u0631\u0641<\/span><\/p>\n<p><strong>\u0627\u0644\u0645\u0635\u062f\u0631<\/strong>:<\/p>\n<p><a href=\"https:\/\/www.sciencenews.org\/article\/gene-therapy-sickle-cell-disease-esrick-genetics\">https:\/\/www.sciencenews.org\/article\/gene-therapy-sickle-cell-disease-esrick-genetics<\/a><\/p>\n<p><strong>\u0627\u0644\u0647\u0648\u0627\u0645\u0634:<\/strong><\/p>\n<p><span style=\"font-size: 10pt;\">[\u0661] \u064a\u0648\u0641\u0631 \u062c\u064a\u0646 \u0648\u062d\u062f\u0629 \u0627\u0644\u0647\u064a\u0645\u0648\u063a\u0644\u0648\u0628\u064a\u0646 \u0627\u0644\u0641\u0631\u0639\u064a\u0629 \u0628\u064a\u062a\u0627 [Hemoglobin Subunit Beta (HBB)] \u062a\u0639\u0644\u064a\u0645\u0627\u062a \u0644\u0635\u0646\u0639 \u0628\u0631\u0648\u062a\u064a\u0646 \u064a\u0633\u0645\u0649 \u0628\u064a\u062a\u0627-\u063a\u0644\u0648\u0628\u064a\u0646 (beta-globin)\u060c \u0648\u0647\u0648 \u0645\u0643\u0648\u0646 (\u0648\u062d\u062f\u0629 \u0641\u0631\u0639\u064a\u0629) \u0645\u0646 \u0628\u0631\u0648\u062a\u064a\u0646 \u0623\u0643\u0628\u0631 \u064a\u0633\u0645\u0649 \u0627\u0644\u0647\u064a\u0645\u0648\u063a\u0644\u0648\u0628\u064a\u0646\u060c \u0648\u0627\u0644\u0630\u064a \u064a\u0642\u0639 \u062f\u0627\u062e\u0644 \u062e\u0644\u0627\u064a\u0627 \u0627\u0644\u062f\u0645 \u0627\u0644\u062d\u0645\u0631\u0627\u0621. \u0648\u0641\u064a \u0627\u0644\u0628\u0627\u0644\u063a\u064a\u0646\u060c \u064a\u062a\u0643\u0648\u0646 \u0627\u0644\u0647\u064a\u0645\u0648\u063a\u0644\u0648\u0628\u064a\u0646 \u0639\u0627\u062f\u0629 \u0645\u0646 \u0623\u0631\u0628\u0639 \u0648\u062d\u062f\u0627\u062a \u0641\u0631\u0639\u064a\u0629 \u0645\u0646 \u0627\u0644\u0628\u0631\u0648\u062a\u064a\u0646: \u0648\u062d\u062f\u062a\u0627\u0646 \u0641\u0631\u0639\u064a\u062a\u0627\u0646 \u0645\u0646 \u0628\u064a\u062a\u0627 \u063a\u0644\u0648\u0628\u064a\u0646 \u0648\u0648\u062d\u062f\u062a\u0627\u0646 \u0641\u0631\u0639\u064a\u062a\u0627\u0646 \u0645\u0646 \u0628\u0631\u0648\u062a\u064a\u0646 \u064a\u0633\u0645\u0649 \u0623\u0644\u0641\u0627 \u063a\u0644\u0648\u0628\u064a\u0646\u060c \u0648\u0627\u0644\u0630\u064a \u064a\u062a\u0645 \u0625\u0646\u062a\u0627\u062c\u0647 \u0645\u0646 \u062c\u064a\u0646 \u0622\u062e\u0631 \u064a\u0633\u0645\u0649 \u0627\u0644\u0647\u064a\u0645\u0648\u063a\u0644\u0648\u0628\u064a\u0646 \u0627\u0644\u0641\u0631\u0639\u064a\u0629 \u0623\u0644\u0641\u0627 (HBA). \u062a\u0631\u062a\u0628\u0637 \u0643\u0644 \u0648\u062d\u062f\u0629 \u0645\u0646 \u0647\u0630\u0647 \u0627\u0644\u0648\u062d\u062f\u0627\u062a \u0627\u0644\u0641\u0631\u0639\u064a\u0629 \u0627\u0644\u0628\u0631\u0648\u062a\u064a\u0646\u064a\u0629 (\u0645\u0631\u062a\u0628\u0637\u0629) \u0628\u062c\u0632\u064a\u0621 \u064a\u062d\u062a\u0648\u064a \u0639\u0644\u0649 \u0627\u0644\u062d\u062f\u064a\u062f \u064a\u0633\u0645\u0649 \u0627\u0644\u0647\u064a\u0645 (heme)\u061b \u064a\u062d\u062a\u0648\u064a \u0639\u0644\u0649 \u062c\u0632\u064a\u0621 \u062d\u062f\u064a\u062f\u064a \u0641\u064a \u0645\u0631\u0643\u0632\u0647 \u064a\u0645\u0643\u0646 \u0623\u0646 \u064a\u0631\u062a\u0628\u0637 \u0628\u062c\u0632\u064a\u0621 \u0623\u0643\u0633\u062c\u064a\u0646 \u0648\u0627\u062d\u062f. \u064a\u0631\u062a\u0628\u0637 \u0627\u0644\u0647\u064a\u0645\u0648\u062c\u0644\u0648\u0628\u064a\u0646 \u062f\u0627\u062e\u0644 \u062e\u0644\u0627\u064a\u0627 \u0627\u0644\u062f\u0645 \u0627\u0644\u062d\u0645\u0631\u0627\u0621 \u0628\u062c\u0632\u064a\u0626\u0627\u062a \u0627\u0644\u0623\u0643\u0633\u062c\u064a\u0646 \u0641\u064a \u0627\u0644\u0631\u0626\u062a\u064a\u0646. \u062b\u0645 \u062a\u0646\u062a\u0642\u0644 \u0647\u0630\u0647 \u0627\u0644\u062e\u0644\u0627\u064a\u0627 \u0639\u0628\u0631 \u0645\u062c\u0631\u0649 \u0627\u0644\u062f\u0645 \u0648\u062a\u0646\u0642\u0644 \u0627\u0644\u0623\u0643\u0633\u062c\u064a\u0646 \u0625\u0644\u0649 \u0627\u0644\u0623\u0646\u0633\u062c\u0629 \u0641\u064a \u062c\u0645\u064a\u0639 \u0623\u0646\u062d\u0627\u0621 \u0627\u0644\u062c\u0633\u0645. \u0627\u0644\u0645\u0635\u062f\u0631: <a href=\"https:\/\/medlineplus.gov\/genetics\/gene\/hbb\/\">https:\/\/medlineplus.gov\/genetics\/gene\/hbb\/<\/a><\/span><\/p>\n<p><span style=\"font-size: 10pt;\">[\u0662] \u0643\u0631\u064a\u0633\u0628\u0631-\u0643\u0627\u06339 \u0647\u064a \u062a\u0642\u0646\u064a\u0629 \u0641\u0631\u064a\u062f\u0629 \u062a\u0645\u0643\u0646 \u0639\u0644\u0645\u0627\u0621 \u0627\u0644\u0648\u0631\u0627\u062b\u0629 \u0648\u0627\u0644\u0628\u0627\u062d\u062b\u064a\u0646 \u0627\u0644\u0637\u0628\u064a\u064a\u0646 \u0645\u0646 \u062a\u062d\u0631\u064a\u0631 \u0623\u062c\u0632\u0627\u0621 \u0645\u0646 \u0627\u0644\u062c\u064a\u0646\u0648\u0645 \u0639\u0646 \u0637\u0631\u064a\u0642 \u0625\u0632\u0627\u0644\u0629 \u0623\u0648 \u0625\u0636\u0627\u0641\u0629 \u0623\u0648 \u062a\u063a\u064a\u064a\u0631 \u0623\u062c\u0632\u0627\u0621 \u0645\u0646 \u062a\u0633\u0644\u0633\u0644 \u0627\u0644\u062d\u0645\u0636 \u0627\u0644\u0646\u0648\u0648\u064a. \u0625\u0646\u0647\u0627 \u062d\u0627\u0644\u064a\u0627 \u0627\u0644\u0637\u0631\u064a\u0642\u0629 \u0627\u0644\u0623\u0628\u0633\u0637 \u0648\u0627\u0644\u0623\u0643\u062b\u0631 \u062a\u0646\u0648\u0639\u0627 \u0648\u062f\u0642\u0629 \u0644\u0644\u062a\u0644\u0627\u0639\u0628 \u0627\u0644\u062c\u064a\u0646\u064a\u060c \u0648\u0628\u0627\u0644\u062a\u0627\u0644\u064a \u0641\u0647\u064a \u062a\u0633\u0628\u0628 \u0636\u062c\u0629 \u0641\u064a \u0639\u0627\u0644\u0645 \u0627\u0644\u0639\u0644\u0648\u0645. \u064a\u062a\u0643\u0648\u0646 \u0646\u0638\u0627\u0645 \u0643\u0631\u064a\u0633\u0628\u0631-\u0643\u0627\u06339 \u0645\u0646 \u062c\u0632\u064a\u0626\u064a\u0646 \u0631\u0626\u064a\u0633\u064a\u064a\u0646 \u064a\u062f\u062e\u0644\u0627\u0646 \u062a\u063a\u064a\u064a\u0631\u0627 (\u0637\u0641\u0631\u0629) \u0641\u064a \u0627\u0644\u062d\u0645\u0636 \u0627\u0644\u0646\u0648\u0648\u064a. \u0648\u0647\u064a:<\/span><\/p>\n<ul>\n<li><span style=\"font-size: 10pt;\">\u0625\u0646\u0632\u064a\u0645 \u064a\u0633\u0645\u0649 (Cas9) \u064a\u0639\u0645\u0644 \u0643\u0632\u0648\u062c \u0645\u0646 &#8220;\u0627\u0644\u0645\u0642\u0635 \u0627\u0644\u062c\u0632\u064a\u0626\u064a&#8221; \u0627\u0644\u0630\u064a \u064a\u0645\u0643\u0646\u0647 \u0642\u0637\u0639 \u0634\u0642\u064a \u0627\u0644\u062d\u0645\u0636 \u0627\u0644\u0646\u0648\u0648\u064a \u0641\u064a \u0645\u0648\u0642\u0639 \u0645\u0639\u064a\u0646 \u0641\u064a \u0627\u0644\u062c\u064a\u0646\u0648\u0645 \u0628\u062d\u064a\u062b \u064a\u0645\u0643\u0646 \u0628\u0639\u062f \u0630\u0644\u0643 \u0625\u0636\u0627\u0641\u0629 \u0623\u062c\u0632\u0627\u0621 \u0645\u0646 \u0627\u0644\u062d\u0645\u0636 \u0627\u0644\u0646\u0648\u0648\u064a \u0623\u0648 \u0625\u0632\u0627\u0644\u062a\u0647\u0627.<\/span><\/li>\n<li><span style=\"font-size: 10pt;\">\u0642\u0637\u0639\u0629 \u0645\u0646 \u0627\u0644\u062d\u0645\u0636 \u0627\u0644\u0646\u0648\u0648\u064a \u0627\u0644\u0631\u064a\u0628\u064a \u064a\u0633\u0645\u0649 \u062f\u0644\u064a\u0644 \u0627\u0644\u062d\u0645\u0636 \u0627\u0644\u0646\u0648\u0648\u064a \u0627\u0644\u0631\u064a\u0628\u064a (gRNA). \u064a\u062a\u0643\u0648\u0646 \u0647\u0630\u0627 \u0645\u0646 \u0642\u0637\u0639\u0629 \u0635\u063a\u064a\u0631\u0629 \u0645\u0646 \u062a\u0633\u0644\u0633\u0644 \u0627\u0644\u062d\u0645\u0636 \u0627\u0644\u0646\u0648\u0648\u064a \u0627\u0644\u0631\u064a\u0628\u064a \u0627\u0644\u0645\u0635\u0645\u0645 \u0645\u0633\u0628\u0642\u0627 (\u0637\u0648\u0644\u0647 \u062d\u0648\u0627\u0644\u064a 20 \u0642\u0627\u0639\u062f\u0629) \u062a\u0642\u0639 \u062f\u0627\u062e\u0644 \u0633\u0642\u0627\u0644\u0629 \u0627\u0644\u062d\u0645\u0636 \u0627\u0644\u0646\u0648\u0648\u064a \u0627\u0644\u0631\u064a\u0628\u064a \u0627\u0644\u0623\u0637\u0648\u0644. \u064a\u0631\u062a\u0628\u0637 \u062c\u0632\u0621 \u0627\u0644\u0633\u0642\u0627\u0644\u0629 \u0628\u0627\u0644\u062d\u0645\u0636 \u0627\u0644\u0646\u0648\u0648\u064a \u0648\u0627\u0644\u062a\u0633\u0644\u0633\u0644 \u0627\u0644\u0645\u0635\u0645\u0645 \u0645\u0633\u0628\u0642\u0627 &#8220;\u064a\u0648\u062c\u0647&#8221; (Cas9) \u0625\u0644\u0649 \u0627\u0644\u062c\u0632\u0621 \u0627\u0644\u0623\u064a\u0645\u0646 \u0645\u0646 \u0627\u0644\u062c\u064a\u0646\u0648\u0645. \u0647\u0630\u0627 \u064a\u0636\u0645\u0646 \u0623\u0646 \u0625\u0646\u0632\u064a\u0645 (Cas9) \u064a\u0642\u0637\u0639 \u0639\u0646\u062f \u0627\u0644\u0646\u0642\u0637\u0629 \u0627\u0644\u0635\u062d\u064a\u062d\u0629 \u0641\u064a \u0627\u0644\u062c\u064a\u0646\u0648\u0645.<\/span><\/li>\n<li><span style=\"font-size: 10pt;\">\u062a\u0645 \u062a\u0635\u0645\u064a\u0645 \u0627\u0644\u062d\u0645\u0636 \u0627\u0644\u0646\u0648\u0648\u064a \u0627\u0644\u0631\u064a\u0628\u064a \u0627\u0644\u062f\u0644\u064a\u0644\u064a \u0644\u0644\u0639\u062b\u0648\u0631 \u0639\u0644\u0649 \u062a\u0633\u0644\u0633\u0644 \u0645\u062d\u062f\u062f \u0641\u064a \u0627\u0644\u062d\u0645\u0636 \u0627\u0644\u0646\u0648\u0648\u064a \u0648\u0627\u0644\u0631\u0628\u0637 \u0628\u0647. \u0647\u0644 \u064a\u062d\u062a\u0648\u064a \u0627\u0644\u062f\u0644\u064a\u0644 \u0627\u0644\u062d\u0645\u0636 \u0627\u0644\u0646\u0648\u0648\u064a \u0627\u0644\u0631\u064a\u0628\u064a \u0639\u0644\u0649 \u0642\u0648\u0627\u0639\u062f \u0627\u0644\u062d\u0645\u0636 \u0627\u0644\u0646\u0648\u0648\u064a \u0627\u0644\u0631\u064a\u0628\u064a\u061f \u0647\u0644 \u0647\u0630\u0627 \u0645\u0643\u0645\u0644\u061f \u0625\u0644\u0649 \u062a\u0633\u0644\u0633\u0644 \u0627\u0644\u062d\u0645\u0636 \u0627\u0644\u0646\u0648\u0648\u064a \u0627\u0644\u0645\u0633\u062a\u0647\u062f\u0641 \u0641\u064a \u0627\u0644\u062c\u064a\u0646\u0648\u0645. \u0647\u0630\u0627 \u064a\u0639\u0646\u064a \u0623\u0646\u0647\u060c \u0639\u0644\u0649 \u0627\u0644\u0623\u0642\u0644 \u0645\u0646 \u0627\u0644\u0646\u0627\u062d\u064a\u0629 \u0627\u0644\u0646\u0638\u0631\u064a\u0629\u060c \u0644\u0646 \u064a\u0631\u062a\u0628\u0637 \u0627\u0644\u062d\u0645\u0636 \u0627\u0644\u0646\u0648\u0648\u064a \u0627\u0644\u0631\u064a\u0628\u064a \u0627\u0644\u0645\u0631\u0634\u062f \u0625\u0644\u0627 \u0628\u0627\u0644\u062a\u0633\u0644\u0633\u0644 \u0627\u0644\u0645\u0633\u062a\u0647\u062f\u0641 \u0648\u0644\u0627 \u062a\u0648\u062c\u062f \u0645\u0646\u0627\u0637\u0642 \u0623\u062e\u0631\u0649 \u0645\u0646 \u0627\u0644\u062c\u064a\u0646\u0648\u0645.<\/span><\/li>\n<li><span style=\"font-size: 10pt;\">\u064a\u062a\u0628\u0639 (Cas9) \u062f\u0644\u064a\u0644 \u0627\u0644\u062d\u0645\u0636 \u0627\u0644\u0646\u0648\u0648\u064a \u0627\u0644\u0631\u064a\u0628\u064a \u0625\u0644\u0649 \u0646\u0641\u0633 \u0627\u0644\u0645\u0648\u0642\u0639 \u0641\u064a \u062a\u0633\u0644\u0633\u0644 \u0627\u0644\u062d\u0645\u0636 \u0627\u0644\u0646\u0648\u0648\u064a \u0648\u064a\u0642\u0648\u0645 \u0628\u0642\u0637\u0639 \u0643\u0644\u0627 \u062e\u064a\u0648\u0637 \u0627\u0644\u062d\u0645\u0636 \u0627\u0644\u0646\u0648\u0648\u064a.<\/span><\/li>\n<li><span style=\"font-size: 10pt;\">\u0641\u064a \u0647\u0630\u0647 \u0627\u0644\u0645\u0631\u062d\u0644\u0629 \u062a\u062f\u0631\u0643 \u0627\u0644\u062e\u0644\u064a\u0629 \u0623\u0646 \u0627\u0644\u062d\u0645\u0636 \u0627\u0644\u0646\u0648\u0648\u064a \u062a\u0627\u0644\u0641 \u0648\u064a\u062d\u0627\u0648\u0644 \u0625\u0635\u0644\u0627\u062d\u0647.<\/span><\/li>\n<\/ul>\n<p><span style=\"font-size: 10pt;\">\u0627\u0644\u0645\u0635\u062f\u0631: <a href=\"https:\/\/www.yourgenome.org\/facts\/what-is-crispr-cas9\">https:\/\/www.yourgenome.org\/facts\/what-is-crispr-cas9<\/a><\/span><\/p>\n<p><span style=\"font-size: 10pt;\">[\u0663] \u0627\u0644\u062a\u0637\u0639\u064a\u0645 \u0645\u0642\u0627\u0628\u0644 \u0645\u0631\u0636 \u0627\u0644\u0645\u0636\u064a\u0641 (GvHD) \u0647\u0648 \u062d\u0627\u0644\u0629 \u0642\u062f \u062a\u062d\u062f\u062b \u0628\u0639\u062f \u0639\u0645\u0644\u064a\u0629 \u0632\u0631\u0639 \u062e\u064a\u0641\u064a [\u062a\u0634\u064a\u0631 \u0627\u0644\u0649 \u0623\u0646\u0633\u062c\u0629 \u0623\u0648 \u062e\u0644\u0627\u064a\u0627 \u063a\u064a\u0631 \u0645\u062a\u0634\u0627\u0628\u0647\u0629 \u0648\u0631\u0627\u062b\u064a\u0627 \u0648\u0628\u0627\u0644\u062a\u0627\u0644\u064a \u063a\u064a\u0631 \u0645\u062a\u0648\u0627\u0641\u0642\u0629 \u0645\u0646\u0627\u0639\u064a\u0627\u060c \u0627\u0648 \u062a\u062a\u0639\u0644\u0642 \u0628\u0647\u0627\u060c \u0627\u0648 \u062a\u062a\u0636\u0645\u0646\u0647\u0627\u060c \u0639\u0644\u0649 \u0627\u0644\u0631\u063a\u0645 \u0645\u0646 \u0623\u0646\u0647\u0627 \u0645\u0646 \u0623\u0641\u0631\u0627\u062f \u0645\u0646 \u0646\u0641\u0633 \u0627\u0644\u0646\u0648\u0639]. \u0641\u064a \u0627\u0644\u062a\u0637\u0639\u064a\u0645 \u0645\u0642\u0627\u0628\u0644 \u0645\u0631\u0636 \u0627\u0644\u0645\u0636\u064a\u0641\u060c \u064a\u0646\u0638\u0631 \u0646\u062e\u0627\u0639 \u0627\u0644\u0639\u0638\u0627\u0645 \u0627\u0644\u0645\u062a\u0628\u0631\u0639 \u0628\u0647 \u0623\u0648 \u0627\u0644\u062e\u0644\u0627\u064a\u0627 \u0627\u0644\u062c\u0630\u0639\u064a\u0629 \u0644\u0644\u062f\u0645 \u0627\u0644\u0645\u062d\u064a\u0637\u064a \u0625\u0644\u0649 \u062c\u0633\u0645 \u0627\u0644\u0645\u062a\u0644\u0642\u064a \u0639\u0644\u0649 \u0623\u0646\u0647 \u063a\u0631\u064a\u0628\u060c \u0648\u062a\u0647\u0627\u062c\u0645 \u0627\u0644\u062e\u0644\u0627\u064a\u0627 \/ \u0646\u062e\u0627\u0639 \u0627\u0644\u0639\u0638\u0627\u0645 \u0627\u0644\u0645\u062a\u0628\u0631\u0639 \u0628\u0647 \u0627\u0644\u062c\u0633\u0645. \u0647\u0646\u0627\u0643 \u0646\u0648\u0639\u0627\u0646 \u0645\u0646 \u0623\u0634\u0643\u0627\u0644 \u0627\u0644\u062a\u0637\u0639\u064a\u0645 \u0645\u0642\u0627\u0628\u0644 \u0645\u0631\u0636 \u0627\u0644\u0645\u0636\u064a\u0641:<\/span><\/p>\n<ul>\n<li><span style=\"font-size: 10pt;\">\u0627\u0644\u062a\u0637\u0639\u064a\u0645 \u0627\u0644\u062d\u0627\u062f \u0645\u0642\u0627\u0628\u0644 \u0645\u0631\u0636 \u0627\u0644\u0645\u0636\u064a\u0641 (aGvHD).<\/span><\/li>\n<li><span style=\"font-size: 10pt;\">\u0627\u0644\u062a\u0637\u0639\u064a\u0645 \u0627\u0644\u0645\u0632\u0645\u0646 \u0645\u0642\u0627\u0628\u0644 \u0645\u0631\u0636 \u0627\u0644\u0645\u0636\u064a\u0641 (cGvHD).<\/span><\/li>\n<\/ul>\n<p><span style=\"font-size: 10pt;\">\u0628\u0635\u0641\u062a\u0643 \u0645\u062a\u0644\u0642\u064a \u0632\u0631\u0639 \u062e\u064a\u0641\u060c \u0642\u062f \u062a\u0648\u0627\u062c\u0647 \u0623\u064a\u0627 \u0645\u0646 \u0623\u0634\u0643\u0627\u0644 \u0627\u0644\u062a\u0637\u0639\u064a\u0645 \u0645\u0642\u0627\u0628\u0644 \u0645\u0631\u0636 \u0627\u0644\u0645\u0636\u064a\u0641\u060c \u0643\u0644\u0627 \u0627\u0644\u0634\u0643\u0644\u064a\u0646\u060c \u0623\u0648 \u0644\u0627.<\/span><\/p>\n<p><span style=\"font-size: 10pt;\">\u0627\u0644\u0645\u0635\u062f\u0631: <a href=\"https:\/\/my.clevelandclinic.org\/health\/diseases\/10255-graft-vs-host-disease-an-overview-in-bone-marrow-transplant\">https:\/\/my.clevelandclinic.org\/health\/diseases\/10255-graft-vs-host-disease-an-overview-in-bone-marrow-transplant<\/a><\/span><\/p>\n<figure id=\"attachment_13472\" aria-describedby=\"caption-attachment-13472\" style=\"width: 114px\" class=\"wp-caption aligncenter\"><img loading=\"lazy\" decoding=\"async\" class=\" wp-image-13472\" src=\"https:\/\/www.qatifscience.com\/wp-content\/uploads\/2021\/11\/\u0645\u062d\u0645\u062f-\u062c\u0648\u0627\u062f-227x300.jpg\" alt=\"\" width=\"114\" height=\"151\" srcset=\"https:\/\/www.qatifscience.com\/wp-content\/uploads\/2021\/11\/\u0645\u062d\u0645\u062f-\u062c\u0648\u0627\u062f-227x300.jpg 227w, https:\/\/www.qatifscience.com\/wp-content\/uploads\/2021\/11\/\u0645\u062d\u0645\u062f-\u062c\u0648\u0627\u062f-114x150.jpg 114w, https:\/\/www.qatifscience.com\/wp-content\/uploads\/2021\/11\/\u0645\u062d\u0645\u062f-\u062c\u0648\u0627\u062f-57x75.jpg 57w, https:\/\/www.qatifscience.com\/wp-content\/uploads\/2021\/11\/\u0645\u062d\u0645\u062f-\u062c\u0648\u0627\u062f-125x165.jpg 125w, https:\/\/www.qatifscience.com\/wp-content\/uploads\/2021\/11\/\u0645\u062d\u0645\u062f-\u062c\u0648\u0627\u062f-155x205.jpg 155w, https:\/\/www.qatifscience.com\/wp-content\/uploads\/2021\/11\/\u0645\u062d\u0645\u062f-\u062c\u0648\u0627\u062f.jpg 250w\" sizes=\"auto, (max-width: 114px) 100vw, 114px\" \/><figcaption id=\"caption-attachment-13472\" class=\"wp-caption-text\"><span style=\"color: #0000ff; font-size: 8pt;\">\u0627\u0644\u0645\u0647\u0646\u062f\u0633 \u0645\u062d\u0645\u062f \u062c\u0648\u0627\u062f \u0622\u0644 \u0627\u0644\u0633\u064a\u062f \u0646\u0627\u0635\u0631 \u0627\u0644\u062e\u0636\u0631\u0627\u0648\u064a<\/span><\/figcaption><\/figure>\n","protected":false},"excerpt":{"rendered":"<p>Gene therapies for sickle cell disease come with hope and challenges (Erin Garcia Jesus &#8211; \u0628\u0642\u0644\u0645: \u0625\u064a\u0631\u064a\u0646 \u063a\u0627\u0631\u0633\u064a\u0627 \u062f\u064a \u062e\u064a\u0633\u0648\u0633) \u0645\u0644\u062e\u0635 \u0627\u0644\u0645\u0642\u0627\u0644\u0629: \u0631\u063a\u0645 \u0623\u0646 \u062c\u064a\u0646\u0627\u062a\u0646\u0627 \u062a\u0633\u0628\u0628 \u0627\u0644\u0639\u062f\u064a\u062f \u0645\u0646 \u0627\u0644\u0623\u0645\u0631\u0627\u0636\u060c \u0627\u0644\u0627 \u0623\u0646\u0647\u0627 \u062a\u062d\u0645\u0644 \u0623\u064a\u0636\u0627 \u0639\u0644\u0627\u062c\u0627\u062a \u0645\u062d\u062a\u0645\u0644\u0629 \u0639\u0646 \u0637\u0631\u064a\u0642 \u0627\u0633\u062a\u0628\u062f\u0627\u0644 \u0627\u0644\u062c\u064a\u0646\u0627\u062a \u0627\u0644\u0645\u0641\u0642\u0648\u062f\u0629 \u0623\u0648 \u0627\u0644\u062a\u0627\u0644\u0641\u0629 \u0623\u0648 \u062a\u0639\u0637\u064a\u0644\u0647\u0627 \u0623\u0648 \u0625\u0635\u0644\u0627\u062d\u0647\u0627 &#8211; \u0648\u0628\u0627\u0644\u062a\u0627\u0644\u064a \u0639\u0644\u0627\u062c \u0627\u0644\u0645\u0631\u0636\u0649. \u0648\u0627\u0644\u064a\u0648\u0645 \u0648\u0628\u0639\u062f \u0645\u0627 \u064a\u0642\u0631\u0628 \u0645\u0646 &hellip;<\/p>\n","protected":false},"author":4,"featured_media":15347,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"_exactmetrics_skip_tracking":false,"_exactmetrics_sitenote_active":false,"_exactmetrics_sitenote_note":"","_exactmetrics_sitenote_category":0,"footnotes":""},"categories":[19],"tags":[],"class_list":["post-15344","post","type-post","status-publish","format-standard","has-post-thumbnail","","category-19"],"_links":{"self":[{"href":"https:\/\/www.qatifscience.com\/index.php?rest_route=\/wp\/v2\/posts\/15344","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/www.qatifscience.com\/index.php?rest_route=\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/www.qatifscience.com\/index.php?rest_route=\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/www.qatifscience.com\/index.php?rest_route=\/wp\/v2\/users\/4"}],"replies":[{"embeddable":true,"href":"https:\/\/www.qatifscience.com\/index.php?rest_route=%2Fwp%2Fv2%2Fcomments&post=15344"}],"version-history":[{"count":2,"href":"https:\/\/www.qatifscience.com\/index.php?rest_route=\/wp\/v2\/posts\/15344\/revisions"}],"predecessor-version":[{"id":15349,"href":"https:\/\/www.qatifscience.com\/index.php?rest_route=\/wp\/v2\/posts\/15344\/revisions\/15349"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/www.qatifscience.com\/index.php?rest_route=\/wp\/v2\/media\/15347"}],"wp:attachment":[{"href":"https:\/\/www.qatifscience.com\/index.php?rest_route=%2Fwp%2Fv2%2Fmedia&parent=15344"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/www.qatifscience.com\/index.php?rest_route=%2Fwp%2Fv2%2Fcategories&post=15344"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/www.qatifscience.com\/index.php?rest_route=%2Fwp%2Fv2%2Ftags&post=15344"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}